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JANSSEN BIOTECH — Stelara FDA Review (NDA/BLA 761044, 2021)

Johnson & Johnson · 2021 · FDA Review (Drugs@FDA) · company profile →

Report summary

This FDA approval package details the multidisciplinary review of STELARA (ustekinumab) for ulcerative colitis (UC), building on its existing approvals for other inflammatory conditions. It covers the drug's clinical pharmacology, nonclinical toxicology, and extensive clinical trial results for UC, including induction and maintenance phases. Efficacy was demonstrated through significant clinical remission, response, and mucosal healing rates compared to placebo. The safety profile, consistent across indications, highlights common adverse reactions, serious infections, and malignancies. While the benefit-risk assessment for moderately to severely active UC is favorable, the report emphasizes postmarketing requirements for long-term safety, particularly regarding malignancy risk. Labeling recommendations and dosing regimens are also detailed.

Key findings — cited to the page

Initial intravenous dosage520 mgStelara · p.80
Clinical remission rate19.3 % · p.82
Approval statusapproved Stelara (ustekinumab) · p.80
Initial intravenous dosage390 mgStelara · p.80
Trial duration52 weeks · p.81
Number of patients enrolled961 patients · p.82
Approval statusapproved Stelara (ustekinumab) · p.80
Approval statusapproved Stelara (ustekinumab) · p.80
Approval statusapproved Stelara (ustekinumab) · p.80
Initial intravenous dosage260 mgStelara · p.80
Maintenance dosing90 mgStelara · p.80
Clinical remission rate16.9 % · p.82

Source: Johnson & Johnson · License: US Government public domain. Summary and findings are extracted from the published document; every figure cites its page. Informational only — not investment advice. Explore the Immunology library →

JANSSEN BIOTECH — Stelara FDA Review (NDA/BLA 761044, 2021) — Summary & Key Findings | BioPharmaPT