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Amgen Inc. — Lumakras FDA Review (NDA214665, ORIG 1, 2021)

Amgen Inc. · 2021 · FDA Review (openFDA) · company profile →

Report summary

The FDA's multi-disciplinary review of Amgen's Lumakras (sotorasib) for KRAS G12C-mutated locally advanced or metastatic non-small cell lung cancer (NSCLC) led to accelerated approval. This decision, under Project ORBIS, was based on the CodeBreak 100 study, which demonstrated a 36% objective response rate and a 10-month median duration of response in previously treated patients. Lumakras received Orphan Drug, Fast Track, and Breakthrough Therapy designations. Nonclinical studies identified liver and kidney as target organs for toxicity, with potential embryo-fetal developmental effects at high doses. Pharmacokinetic analyses revealed a non-linear dose-exposure relationship and potential drug-drug interactions. Safety concerns included increased liver enzymes and pneumonitis, addressed in product labeling. The FDA recommended accelerated approval with post-marketing studies to confirm clinical benefit, optimize dosage, and further characterize safety.

Key findings — cited to the page

Grade ≥ 3 adverse events (FDA assessment)59 % · p.189
Grade ≥3 treatment-emergent adverse events58.8 %LUMAKRAS (sotorasib) · p.191
increased ALT (Grade ≥ 3) in NSCLC patients7.8 % · p.189
diarrhea (Grade ≥ 3) in NSCLC patients5.4 % · p.189
pneumonia (Grade ≥ 3, FDA assessment)7 % · p.189
diarrhea (Grade ≥ 3, FDA assessment)5 % · p.189
ALT increased (all grades)20 %Sotorasib 960mg QD in NSCLC · p.199
Grade ≥ 3 adverse events (NSCLC)58.8 % · p.189
increased AST (Grade ≥ 3) in NSCLC patients6.9 % · p.189
pneumonia (Grade ≥ 3) in NSCLC patients6.4 % · p.189
musculoskeletal pain (Grade ≥ 3, FDA assessment)8 % · p.189
Grade ≥3 treatment-related treatment-emergent adverse events20.6 %LUMAKRAS (sotorasib) · p.191

Source: Amgen Inc. · License: US Government public domain. Summary and findings are extracted from the published document; every figure cites its page. Informational only — not investment advice. Explore the Oncology library →

Amgen Inc. — Lumakras FDA Review (NDA214665, ORIG 1, 2021) — Summary & Key Findings | BioPharmaPT