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GSK plc — Zejula EMA EPAR public assessment report (EMEA/H/C/004249, 2017)

GSK plc · 2017 · EMA EPAR public assessment report · company profile →

Report summary

This EMA report details the assessment of Zejula (niraparib) for marketing authorization as a monotherapy for platinum-sensitive recurrent high-grade serous epithelial ovarian, fallopian tube, or primary peritoneal cancer. It covers the regulatory process, orphan designation, and approved indication. The report outlines niraparib's quality control, non-clinical pharmacology (PARP-1/2 inhibition, BRCA-deficient cancer activity), and pharmacokinetic/pharmacodynamic profiles (absorption, distribution, metabolism, excretion). Toxicology studies identified bone marrow and testes as primary target organs. Efficacy and safety data from the pivotal NOVA trial are presented, demonstrating progression-free survival benefits and outlining common adverse events and dose modifications, ultimately supporting a positive benefit-risk profile.

Key findings — cited to the page

Tumour regression rate in orthotopic high-grade serous ovarian cancer PDX models (all models)26 %niraparib · p.22
Tumour regression rate in orthotopic high-grade serous ovarian cancer PDX models (HRD positive models)44 %niraparib · p.22
Tumour shrinkage in BRCA-2mut high grade serous ovarian cancer PDX model36 % of baselineniraparib · p.24
Finished product dosage100 mgniraparib · p.13
EMA/CHMP eligibility agreement date25 June 2015 Zejula · p.7
Confirmation of class waiver for paediatric investigations01 April 2016 niraparib · p.13
Dose300 mgZejula · p.11
Orphan medicinal product designationEU/3/10/760 Zejula · EU · p.7
IC50 for hERG current inhibition10 µMniraparib · p.25
Approved indicationZejula is indicated as monotherapy for the maintenance treatment of adult patients with platinum sensitive relapsed high grade serous epithelial ovarian, fallopian tube, or primary peritoneal cancer who are in response (complete or partial) to platinum based chemotherapy. Zejula · p.11
Oral bioavailability in rats27 %niraparib · p.25
Oral bioavailability in dogs57 %niraparib · p.25

Source: GSK plc · License: EMA - reuse permitted with acknowledgement. Summary and findings are extracted from the published document; every figure cites its page. Informational only — not investment advice. Explore the Oncology library →

GSK plc — Zejula EMA EPAR public assessment report (EMEA/H/C/004249, 2017) — Summary & Key Findings | BioPharmaPT