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Merck & Co., Inc. — Welireg FDA Review (NDA/BLA 215383, 2026)

Merck & Co., Inc. · 2026 · FDA Review (Drugs@FDA) · company profile →

Report summary

Merck & Co., Inc. received FDA approval for WELIREG (belzutifan) on December 14, 2023, for VHL-associated tumors and advanced renal cell carcinoma (RCC). The advanced RCC approval, based on the LITESPARK-005 trial, compared belzutifan to everolimus in patients previously treated with PD-1/PD-L1 inhibitors and VEGF-TKIs. Belzutifan demonstrated statistically significant improvements in progression-free survival (PFS) and objective response rate (ORR) compared to everolimus, with a favorable safety profile. While overall survival (OS) data was immature, it trended positively. The FDA agreed with the study design, including everolimus as a comparator, and found the clinical data reliable. A postmarketing commitment requires final OS analysis from LITESPARK-005. The approval package details drug information, clinical pharmacology, and adverse reactions, with no REMS required.

Key findings — cited to the page

Fatigue (All Grades)64 %LITESPARK-004 · p.14
Nausea (All Grades)31 %LITESPARK-004 · p.14
Decreased hemoglobin (Grade 3 events)7 %WELIREG (belzutifan) · p.12
Hypoxia (Grade 3 events)10 %WELIREG (belzutifan) · p.13
Headache (All Grades)39 %LITESPARK-004 · p.14
Dizziness (All Grades)38 %LITESPARK-004 · p.14
Weight increased (Grade 3-4)1.6 %LITESPARK-004 · p.14
Decreased hemoglobin (all grades)93 %WELIREG (belzutifan) · p.12
Decreased hemoglobin (all grades)88 %WELIREG (belzutifan) · p.12
Decreased hemoglobin (Grade 3 events)29 %WELIREG (belzutifan) · p.12
Fatigue (Grade 3-4)5 %LITESPARK-004 · p.14
Constipation (All Grades)13 %LITESPARK-004 · p.14

Source: Merck & Co., Inc. · License: US Government public domain. Summary and findings are extracted from the published document; every figure cites its page. Informational only — not investment advice. Explore the Oncology library →

Merck & Co., Inc. — Welireg FDA Review (NDA/BLA 215383, 2026) — Summary & Key Findings | BioPharmaPT